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Medical Breakthroughs treating cystic fibrosis

  1. Mar 14, 2009 #1
    http://www.breakthroughdigest.com/lung-diseases/gene-therapy-treatment-for-cystic-fibrosis-sufferers-in-the-works/ [Broken]

    I have a friend who has cystic fibrosis, and she is already 24, with a life expectancy of about 30. Seams that with the ban lifted on stem cell research, and the breakthroughs in gene therapy, she just may live long enough to be cured.

    Anyone have any knowledge of this type of thing? I am trying to find out who/where the leading researchers/ cutting edge innovation is happening, and how if possible to get in line, or possible sign up to be a test subject for something promising.
    Last edited by a moderator: May 4, 2017
  2. jcsd
  3. Mar 15, 2009 #2


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    You should also read this article:
    Thus so far it has only been successfully studied in lung samples in the lab. There is still a lot of work to be done to test whether it work in a clinical setting and whether it is a safe treatment.

    If you are really interested in entering the human trials, you could try and contact the researchers and ask whether that would be possible.
  4. Mar 15, 2009 #3

    Andy Resnick

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    There's a couple of people here specifically trying gene therapy approaches to rescue the CF lung. There are major physiological barriers to transfecting cells in vivo (the mucus layer, the immune response, cell turnover, for example), and the only time (IIRC) this therapy was tried, the patient (18 year old) died.

    There will probably be a flood of proposals in response to the US change in government policy, so it's too soon to tell what may happen. Stay tuned!
  5. Mar 17, 2010 #4
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